Aims: The RUBY trial evaluated the efficacy and safety of dostarlimab+standard of care (SOC) carboplatin paclitaxel (CP) versus CP alone in A/R EC. The primary endpoint of PFS by investigator assessment (INV; RECIST v1.1) was significantly longer with dostarlimab+CP than placebo+CP in the mismatch repair deficient/microsatellite instability-high (dMMR/MSI-H) and overall populations. Here we present the secondary efficacy endpoints by BICR.
Methods: RUBY is a phase 3, global, randomized, double-blind, multicenter, placebo-controlled study (Funded by Tesaro: NCT03981796, GSK: 213361). Patients with primary advanced stage III or IV or first recurrent EC were randomized (1:1) to receive dostarlimab 500 mg or placebo, plus carboplatin AUC 5 and paclitaxel 175 mg/m2 Q3W (6 cycles), followed by dostarlimab 1000 mg or placebo, monotherapy Q6W for up to 3 years. Secondary endpoints by BICR assessment (RECIST v1.1) were PFS, ORR, DOR, and DCR in the dMMR/MSI-H and overall populations.
Results: Of the 494 patients randomized (dostarlimab+CP: 245; placebo+CP: 249), 47.8% had recurrent disease, 18.6% and 33.6% had primary stage III and IV disease, respectively. PFS by BICR was longer with dostarlimab+CP than placebo+CP in the dMMR/MSI-H (HR 0.29; 95% CI 0.158–0.543) and overall populations (HR 0.66; 95% CI 0.517–0.853). ORR and DCR by BICR were similar between the two arms in the two populations. mDOR by BICR was NE (95% CI 13.1–NE) with dostarlimab+CP and 6.9 (5.5–10.1) months with placebo+CP in the dMMR/MSI-H population; 12.9 (8.2–NE) with dostarlimab+CP and 6.7 (5.7–8.3) months with placebo+CP in the overall population. Safety was previously reported.
Conclusions: Dostarlimab+CP showed clinically meaningful improvement in BICR-assessed PFS versus CP alone, in the two populations. HRs for BICR- - and INV-assessed PFS were consistent; benefits seen in all BICR-assessed endpoints were consistent with INV. Dostarlimab+CP represents a new SOC for patients with primary A/R EC.
Originally presented at 2023 ASCO Annual Meeting (10.1200/JCO.2023.41.16_suppl.5503). Permission granted by Wolters Kluwer.